A naturally occurring human minidysferlin protein repairs sarcolemmal lesions in a mouse model of dysferlinopathy.

Krahn, Martin

A naturally occurring human minidysferlin protein repairs sarcolemmal lesions in a mouse model of dysferlinopathy. [electronic resource] - Science translational medicine Sep 2010 - 50ra69 p. digital

Publication Type: Journal Article; Research Support, Non-U.S. Gov't

1946-6242

10.1126/scitranslmed.3000951 doi


Animals
Dependovirus--genetics
Disease Models, Animal
Dysferlin
Genetic Therapy
Humans
Membrane Proteins--genetics
Mice
Muscle Proteins--genetics
Muscular Dystrophies, Limb-Girdle--therapy