A naturally occurring human minidysferlin protein repairs sarcolemmal lesions in a mouse model of dysferlinopathy.
Krahn, Martin
A naturally occurring human minidysferlin protein repairs sarcolemmal lesions in a mouse model of dysferlinopathy. [electronic resource] - Science translational medicine Sep 2010 - 50ra69 p. digital
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
1946-6242
10.1126/scitranslmed.3000951 doi
Animals
Dependovirus--genetics
Disease Models, Animal
Dysferlin
Genetic Therapy
Humans
Membrane Proteins--genetics
Mice
Muscle Proteins--genetics
Muscular Dystrophies, Limb-Girdle--therapy
A naturally occurring human minidysferlin protein repairs sarcolemmal lesions in a mouse model of dysferlinopathy. [electronic resource] - Science translational medicine Sep 2010 - 50ra69 p. digital
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
1946-6242
10.1126/scitranslmed.3000951 doi
Animals
Dependovirus--genetics
Disease Models, Animal
Dysferlin
Genetic Therapy
Humans
Membrane Proteins--genetics
Mice
Muscle Proteins--genetics
Muscular Dystrophies, Limb-Girdle--therapy