Miglustat in adult and juvenile patients with Niemann-Pick disease type C: long-term data from a clinical trial.
Wraith, James E
Miglustat in adult and juvenile patients with Niemann-Pick disease type C: long-term data from a clinical trial. [electronic resource] - Molecular genetics and metabolism Apr 2010 - 351-7 p. digital
Publication Type: Clinical Trial; Journal Article; Research Support, Non-U.S. Gov't
1096-7206
10.1016/j.ymgme.2009.12.006 doi
1-Deoxynojirimycin--adverse effects
Adolescent
Adult
Child
Deglutition--drug effects
Diarrhea--chemically induced
Female
Humans
Niemann-Pick Disease, Type C--drug therapy
Walking
Weight Loss
Miglustat in adult and juvenile patients with Niemann-Pick disease type C: long-term data from a clinical trial. [electronic resource] - Molecular genetics and metabolism Apr 2010 - 351-7 p. digital
Publication Type: Clinical Trial; Journal Article; Research Support, Non-U.S. Gov't
1096-7206
10.1016/j.ymgme.2009.12.006 doi
1-Deoxynojirimycin--adverse effects
Adolescent
Adult
Child
Deglutition--drug effects
Diarrhea--chemically induced
Female
Humans
Niemann-Pick Disease, Type C--drug therapy
Walking
Weight Loss