Gene therapy for homozygous beta-thalassemia. Is it a reality?

Boulad, Farid

Gene therapy for homozygous beta-thalassemia. Is it a reality? [electronic resource] - Hemoglobin 2009 - S188-96 p. digital

Publication Type: Journal Article

1532-432X

10.3109/03630260903351866 doi


Clinical Protocols
Clinical Trials as Topic
Genetic Therapy--methods
Hematopoietic Stem Cell Transplantation--methods
Hematopoietic Stem Cells--metabolism
Homozygote
Humans
Transduction, Genetic
Transplantation Conditioning--methods
beta-Globins--genetics
beta-Thalassemia--genetics