The Jeremiah Metzger Lecture: gene therapy for inherited disorders: from Christmas disease to Leber's amaurosis.

High, Katherine A

The Jeremiah Metzger Lecture: gene therapy for inherited disorders: from Christmas disease to Leber's amaurosis. [electronic resource] - Transactions of the American Clinical and Climatological Association 2009 - 331-59 p. digital

Publication Type: Lecture; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't

0065-7778


Animals
Carrier Proteins--genetics
Dependovirus--genetics
Disease Models, Animal
Dogs
Eye Proteins--genetics
Factor IX--genetics
Female
Genetic Therapy
Genetic Vectors
Hemophilia B--genetics
Humans
Leber Congenital Amaurosis--genetics
Male
cis-trans-Isomerases