Clinical outcomes after long-term treatment with alglucosidase alfa in infants and children with advanced Pompe disease.
Nicolino, Marc
Clinical outcomes after long-term treatment with alglucosidase alfa in infants and children with advanced Pompe disease. [electronic resource] - Genetics in medicine : official journal of the American College of Medical Genetics Mar 2009 - 210-9 p. digital
Publication Type: Clinical Trial; Journal Article; Multicenter Study; Research Support, Non-U.S. Gov't
1530-0366
10.1097/GIM.0b013e31819d0996 doi
Body Height
Body Weight
Child, Preschool
Cough--chemically induced
Echocardiography
Enzyme-Linked Immunosorbent Assay
Female
Glycogen--metabolism
Glycogen Storage Disease Type II--drug therapy
Humans
Immunoglobulin G--blood
Infant
Kaplan-Meier Estimate
Male
Muscle, Skeletal--drug effects
Skin Diseases--chemically induced
Time Factors
Treatment Outcome
alpha-Glucosidases--adverse effects
Clinical outcomes after long-term treatment with alglucosidase alfa in infants and children with advanced Pompe disease. [electronic resource] - Genetics in medicine : official journal of the American College of Medical Genetics Mar 2009 - 210-9 p. digital
Publication Type: Clinical Trial; Journal Article; Multicenter Study; Research Support, Non-U.S. Gov't
1530-0366
10.1097/GIM.0b013e31819d0996 doi
Body Height
Body Weight
Child, Preschool
Cough--chemically induced
Echocardiography
Enzyme-Linked Immunosorbent Assay
Female
Glycogen--metabolism
Glycogen Storage Disease Type II--drug therapy
Humans
Immunoglobulin G--blood
Infant
Kaplan-Meier Estimate
Male
Muscle, Skeletal--drug effects
Skin Diseases--chemically induced
Time Factors
Treatment Outcome
alpha-Glucosidases--adverse effects