Intracerebroventricular infusion of acid sphingomyelinase corrects CNS manifestations in a mouse model of Niemann-Pick A disease.

Dodge, James C

Intracerebroventricular infusion of acid sphingomyelinase corrects CNS manifestations in a mouse model of Niemann-Pick A disease. [electronic resource] - Experimental neurology Feb 2009 - 349-57 p. digital

Publication Type: Journal Article

1090-2430

10.1016/j.expneurol.2008.10.021 doi


Animals
Brain--metabolism
Cholesterol--metabolism
Disease Models, Animal
Humans
Injections, Intraventricular--methods
Lysosomes--drug effects
Mice
Mice, Knockout
Niemann-Pick Disease, Type A--drug therapy
Sphingomyelin Phosphodiesterase--administration & dosage
Sphingomyelins--metabolism
Time Factors