A dose-optimization trial of laronidase (Aldurazyme) in patients with mucopolysaccharidosis I.

Giugliani, Roberto

A dose-optimization trial of laronidase (Aldurazyme) in patients with mucopolysaccharidosis I. [electronic resource] - Molecular genetics and metabolism Jan 2009 - 13-9 p. digital

Publication Type: Journal Article; Multicenter Study; Randomized Controlled Trial; Research Support, Non-U.S. Gov't

1096-7206

10.1016/j.ymgme.2008.10.009 doi


Adolescent
Child
Child, Preschool
Dose-Response Relationship, Drug
Drug Administration Schedule
Female
Glycosaminoglycans--urine
Humans
Iduronidase--administration & dosage
Infusions, Intravenous--adverse effects
Male
Mucopolysaccharidosis I--drug therapy
Young Adult