Correction of ADAMTS13 deficiency by in utero gene transfer of lentiviral vector encoding ADAMTS13 genes.

Niiya, Masami

Correction of ADAMTS13 deficiency by in utero gene transfer of lentiviral vector encoding ADAMTS13 genes. [electronic resource] - Molecular therapy : the journal of the American Society of Gene Therapy Jan 2009 - 34-41 p. digital

Publication Type: Journal Article; Research Support, N.I.H., Extramural

1525-0024

10.1038/mt.2008.223 doi


ADAM Proteins--deficiency
ADAMTS13 Protein
Animals
Blotting, Western
Female
Genetic Therapy--methods
Genetic Vectors--genetics
Humans
Immunoprecipitation
Lentivirus--genetics
Mice
Mice, Mutant Strains
Microscopy, Fluorescence
Purpura, Thrombotic Thrombocytopenic--genetics
Uterus