Doxycycline-controlled splicing modulation by regulated antisense U7 snRNA expression cassettes.

Marquis, J

Doxycycline-controlled splicing modulation by regulated antisense U7 snRNA expression cassettes. [electronic resource] - Gene therapy Jan 2009 - 70-7 p. digital

Publication Type: Journal Article; Research Support, Non-U.S. Gov't

1476-5462

10.1038/gt.2008.138 doi


Alternative Splicing
Doxycycline--pharmacology
Exons
Gene Expression
Gene Expression Regulation--drug effects
Genetic Engineering
Genetic Therapy--methods
HeLa Cells
Humans
Muscular Atrophy, Spinal--genetics
Oligonucleotides, Antisense--genetics
RNA Splicing
RNA, Small Nuclear--genetics
Survival of Motor Neuron 2 Protein--genetics
beta-Globins--genetics
beta-Thalassemia--genetics