Eight years experience with enzyme replacement therapy in two children and one adult with Pompe disease.

van Capelle, C I

Eight years experience with enzyme replacement therapy in two children and one adult with Pompe disease. [electronic resource] - Neuromuscular disorders : NMD Jun 2008 - 447-52 p. digital

Publication Type: Case Reports; Journal Article; Research Support, Non-U.S. Gov't

0960-8966

10.1016/j.nmd.2008.04.009 doi


Adolescent
Adult
Animals
CHO Cells--drug effects
Child
Cricetinae
Cricetulus
Female
Glycogen Storage Disease Type II--drug therapy
Humans
Longitudinal Studies
Male
Muscle, Skeletal--drug effects
Treatment Outcome
alpha-Glucosidases--therapeutic use