Biochemical correction of short-chain acyl-coenzyme A dehydrogenase deficiency after portal vein injection of rAAV8-SCAD.
Beattie, Stuart G
Biochemical correction of short-chain acyl-coenzyme A dehydrogenase deficiency after portal vein injection of rAAV8-SCAD. [electronic resource] - Human gene therapy Jun 2008 - 579-88 p. digital
Publication Type: Journal Article; Research Support, N.I.H., Extramural
1557-7422
10.1089/hum.2007.168 doi
Actins--genetics
Animals
Butyryl-CoA Dehydrogenase--deficiency
Carnitine--analogs & derivatives
Cytomegalovirus--genetics
Dependovirus
Genetic Therapy
Genetic Vectors
Injections, Intravenous
Liver--blood supply
Metabolism, Inborn Errors--therapy
Mice
Mice, Mutant Strains
Portal Vein
Promoter Regions, Genetic
Transduction, Genetic--methods
Biochemical correction of short-chain acyl-coenzyme A dehydrogenase deficiency after portal vein injection of rAAV8-SCAD. [electronic resource] - Human gene therapy Jun 2008 - 579-88 p. digital
Publication Type: Journal Article; Research Support, N.I.H., Extramural
1557-7422
10.1089/hum.2007.168 doi
Actins--genetics
Animals
Butyryl-CoA Dehydrogenase--deficiency
Carnitine--analogs & derivatives
Cytomegalovirus--genetics
Dependovirus
Genetic Therapy
Genetic Vectors
Injections, Intravenous
Liver--blood supply
Metabolism, Inborn Errors--therapy
Mice
Mice, Mutant Strains
Portal Vein
Promoter Regions, Genetic
Transduction, Genetic--methods