Muscle as a target for supplementary factor IX gene transfer.

Hoffman, Brad E

Muscle as a target for supplementary factor IX gene transfer. [electronic resource] - Human gene therapy Jul 2007 - 603-13 p. digital

Publication Type: Journal Article; Research Support, N.I.H., Extramural

1043-0342

10.1089/hum.2007.042 doi


Animals
Antibodies--blood
Dependovirus--genetics
Enzyme-Linked Immunosorbent Assay
Factor IX--genetics
Gene Expression
Genetic Therapy
Genetic Vectors--administration & dosage
Hemophilia B--genetics
Hepatocytes--immunology
Humans
Immune Tolerance
Injections, Intramuscular
Interferon-gamma--blood
Male
Mice
Mice, Inbred C57BL
Muscle, Skeletal--metabolism