Persistent expression of hF.IX After tolerance induction by in utero or neonatal administration of AAV-1-F.IX in hemophilia B mice.

Sabatino, Denise E

Persistent expression of hF.IX After tolerance induction by in utero or neonatal administration of AAV-1-F.IX in hemophilia B mice. [electronic resource] - Molecular therapy : the journal of the American Society of Gene Therapy Sep 2007 - 1677-85 p. digital

Publication Type: Journal Article; Research Support, N.I.H., Extramural

1525-0016

10.1038/sj.mt.6300219 doi


Animals
Animals, Newborn
Capsid--immunology
Dependovirus--genetics
Factor IX--genetics
Female
Fluorescent Antibody Technique
Genetic Therapy--methods
Genetic Vectors--administration & dosage
Hemophilia B--therapy
Humans
Immune Tolerance--immunology
Immunity, Cellular--immunology
Male
Maternal-Fetal Exchange
Mice
Muscles--metabolism
Pregnancy
T-Lymphocytes--immunology