Restoration of SMN function: delivery of a trans-splicing RNA re-directs SMN2 pre-mRNA splicing.
Coady, Tristan H
Restoration of SMN function: delivery of a trans-splicing RNA re-directs SMN2 pre-mRNA splicing. [electronic resource] - Molecular therapy : the journal of the American Society of Gene Therapy Aug 2007 - 1471-8 p. digital
Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
1525-0016
10.1038/sj.mt.6300222 doi
Alternative Splicing--genetics
Base Sequence
Cell Line
Cell Survival
Cyclic AMP Response Element-Binding Protein--genetics
Fibroblasts
Gene Transfer Techniques
Humans
Molecular Sequence Data
Muscular Atrophy, Spinal--genetics
Nerve Tissue Proteins--genetics
RNA, Messenger--genetics
RNA-Binding Proteins--genetics
SMN Complex Proteins
Survival of Motor Neuron 1 Protein
Survival of Motor Neuron 2 Protein
Trans-Splicing--genetics
Transcription, Genetic--genetics
Restoration of SMN function: delivery of a trans-splicing RNA re-directs SMN2 pre-mRNA splicing. [electronic resource] - Molecular therapy : the journal of the American Society of Gene Therapy Aug 2007 - 1471-8 p. digital
Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
1525-0016
10.1038/sj.mt.6300222 doi
Alternative Splicing--genetics
Base Sequence
Cell Line
Cell Survival
Cyclic AMP Response Element-Binding Protein--genetics
Fibroblasts
Gene Transfer Techniques
Humans
Molecular Sequence Data
Muscular Atrophy, Spinal--genetics
Nerve Tissue Proteins--genetics
RNA, Messenger--genetics
RNA-Binding Proteins--genetics
SMN Complex Proteins
Survival of Motor Neuron 1 Protein
Survival of Motor Neuron 2 Protein
Trans-Splicing--genetics
Transcription, Genetic--genetics