Complete correction of enzymatic deficiency and neurochemistry in the GM1-gangliosidosis mouse brain by neonatal adeno-associated virus-mediated gene delivery.
Broekman, M L D
Complete correction of enzymatic deficiency and neurochemistry in the GM1-gangliosidosis mouse brain by neonatal adeno-associated virus-mediated gene delivery. [electronic resource] - Molecular therapy : the journal of the American Society of Gene Therapy Jan 2007 - 30-7 p. digital
Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
1525-0024
10.1038/sj.mt.6300004 doi
Animals
Animals, Newborn
Chromatography, High Pressure Liquid
Dependovirus--genetics
Gangliosidosis, GM1--enzymology
Genetic Therapy
Lipid Metabolism
Lysosomes--enzymology
Mice
Mice, Inbred C57BL
Mice, Knockout
beta-Galactosidase--deficiency
Complete correction of enzymatic deficiency and neurochemistry in the GM1-gangliosidosis mouse brain by neonatal adeno-associated virus-mediated gene delivery. [electronic resource] - Molecular therapy : the journal of the American Society of Gene Therapy Jan 2007 - 30-7 p. digital
Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
1525-0024
10.1038/sj.mt.6300004 doi
Animals
Animals, Newborn
Chromatography, High Pressure Liquid
Dependovirus--genetics
Gangliosidosis, GM1--enzymology
Genetic Therapy
Lipid Metabolism
Lysosomes--enzymology
Mice
Mice, Inbred C57BL
Mice, Knockout
beta-Galactosidase--deficiency