Pompe disease (glycogen storage disease type II): clinical features and enzyme replacement therapy.

van der Beek, N A M E

Pompe disease (glycogen storage disease type II): clinical features and enzyme replacement therapy. [electronic resource] - Acta neurologica Belgica Jun 2006 - 82-6 p. digital

Publication Type: Journal Article; Review

0300-9009


Animals
Glucan 1,4-alpha-Glucosidase--deficiency
Glycogen Storage Disease Type II--drug therapy
Humans
alpha-Glucosidases--deficiency