Impact of 144 weeks of laronidase therapy on body functions, endurance and general well-being in a Hurler-Scheie patient.

Soutar, R L

Impact of 144 weeks of laronidase therapy on body functions, endurance and general well-being in a Hurler-Scheie patient. [electronic resource] - Journal of inherited metabolic disease Aug 2006 - 590 p. digital

Publication Type: Case Reports; Journal Article

1573-2665

10.1007/s10545-006-0329-5 doi


Adolescent
Female
Humans
Iduronidase--administration & dosage
Mucopolysaccharidosis I--drug therapy
Quality of Life
Recombinant Proteins--administration & dosage