Gene therapy advances but struggles to interpret safety data in small animal models.
Williams, David A
Gene therapy advances but struggles to interpret safety data in small animal models. [electronic resource] - Molecular therapy : the journal of the American Society of Gene Therapy Jun 2006 - 1027-8 p. digital
Publication Type: Editorial
1525-0016
10.1016/j.ymthe.2006.05.001 doi
Adenosine Deaminase--deficiency
Animals
Clinical Trials as Topic
DNA-Binding Proteins--genetics
Deficiency Diseases--genetics
Disease Models, Animal
Gene Expression Regulation
Genetic Therapy--methods
Granulomatous Disease, Chronic--genetics
Humans
Interleukin Receptor Common gamma Subunit
MDS1 and EVI1 Complex Locus Protein
Mice
Neoplasm Proteins--genetics
Proto-Oncogenes
Receptors, Interleukin--genetics
Severe Combined Immunodeficiency--genetics
Transcription Factors--genetics
Gene therapy advances but struggles to interpret safety data in small animal models. [electronic resource] - Molecular therapy : the journal of the American Society of Gene Therapy Jun 2006 - 1027-8 p. digital
Publication Type: Editorial
1525-0016
10.1016/j.ymthe.2006.05.001 doi
Adenosine Deaminase--deficiency
Animals
Clinical Trials as Topic
DNA-Binding Proteins--genetics
Deficiency Diseases--genetics
Disease Models, Animal
Gene Expression Regulation
Genetic Therapy--methods
Granulomatous Disease, Chronic--genetics
Humans
Interleukin Receptor Common gamma Subunit
MDS1 and EVI1 Complex Locus Protein
Mice
Neoplasm Proteins--genetics
Proto-Oncogenes
Receptors, Interleukin--genetics
Severe Combined Immunodeficiency--genetics
Transcription Factors--genetics