Stimulating full-length SMN2 expression by delivering bifunctional RNAs via a viral vector.
Baughan, Travis
Stimulating full-length SMN2 expression by delivering bifunctional RNAs via a viral vector. [electronic resource] - Molecular therapy : the journal of the American Society of Gene Therapy Jul 2006 - 54-62 p. digital
Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
1525-0016
10.1016/j.ymthe.2006.01.012 doi
Blotting, Western
Cells, Cultured
Cyclic AMP Response Element-Binding Protein--genetics
Dependovirus--genetics
Exons--genetics
Fibroblasts--metabolism
Genetic Vectors--genetics
HeLa Cells
Humans
Luciferases--genetics
Microscopy, Fluorescence
Models, Genetic
Muscular Atrophy, Spinal--genetics
Nerve Tissue Proteins--genetics
RNA--genetics
RNA Precursors--genetics
RNA Splicing--genetics
RNA-Binding Proteins--genetics
Reverse Transcriptase Polymerase Chain Reaction
SMN Complex Proteins
Survival of Motor Neuron 1 Protein
Survival of Motor Neuron 2 Protein
Transfection--methods
Stimulating full-length SMN2 expression by delivering bifunctional RNAs via a viral vector. [electronic resource] - Molecular therapy : the journal of the American Society of Gene Therapy Jul 2006 - 54-62 p. digital
Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
1525-0016
10.1016/j.ymthe.2006.01.012 doi
Blotting, Western
Cells, Cultured
Cyclic AMP Response Element-Binding Protein--genetics
Dependovirus--genetics
Exons--genetics
Fibroblasts--metabolism
Genetic Vectors--genetics
HeLa Cells
Humans
Luciferases--genetics
Microscopy, Fluorescence
Models, Genetic
Muscular Atrophy, Spinal--genetics
Nerve Tissue Proteins--genetics
RNA--genetics
RNA Precursors--genetics
RNA Splicing--genetics
RNA-Binding Proteins--genetics
Reverse Transcriptase Polymerase Chain Reaction
SMN Complex Proteins
Survival of Motor Neuron 1 Protein
Survival of Motor Neuron 2 Protein
Transfection--methods