AAV2-mediated CLN2 gene transfer to rodent and non-human primate brain results in long-term TPP-I expression compatible with therapy for LINCL.
Sondhi, D
AAV2-mediated CLN2 gene transfer to rodent and non-human primate brain results in long-term TPP-I expression compatible with therapy for LINCL. [electronic resource] - Gene therapy Nov 2005 - 1618-32 p. digital
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
0969-7128
10.1038/sj.gt.3302549 doi
Aminopeptidases
Animals
Brain--metabolism
Chlorocebus aethiops
Dependovirus--genetics
Dipeptidyl-Peptidases and Tripeptidyl-Peptidases
Endopeptidases--analysis
Gene Expression
Genes, Recessive
Genetic Therapy--methods
Genetic Vectors--administration & dosage
Humans
Immunoenzyme Techniques
Male
Microinjections
Models, Animal
Neuronal Ceroid-Lipofuscinoses--metabolism
Rats
Rats, Inbred F344
Serine Proteases
Time Factors
Tripeptidyl-Peptidase 1
AAV2-mediated CLN2 gene transfer to rodent and non-human primate brain results in long-term TPP-I expression compatible with therapy for LINCL. [electronic resource] - Gene therapy Nov 2005 - 1618-32 p. digital
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
0969-7128
10.1038/sj.gt.3302549 doi
Aminopeptidases
Animals
Brain--metabolism
Chlorocebus aethiops
Dependovirus--genetics
Dipeptidyl-Peptidases and Tripeptidyl-Peptidases
Endopeptidases--analysis
Gene Expression
Genes, Recessive
Genetic Therapy--methods
Genetic Vectors--administration & dosage
Humans
Immunoenzyme Techniques
Male
Microinjections
Models, Animal
Neuronal Ceroid-Lipofuscinoses--metabolism
Rats
Rats, Inbred F344
Serine Proteases
Time Factors
Tripeptidyl-Peptidase 1