Enzyme replacement therapy in mucopolysaccharidosis type I.

Miebach, E

Enzyme replacement therapy in mucopolysaccharidosis type I. [electronic resource] - Acta paediatrica (Oslo, Norway : 1992). Supplement Mar 2005 - 58-60; discussion 57 p. digital

Publication Type: Journal Article; Review

0803-5326

10.1111/j.1651-2227.2005.tb02114.x doi


Bone Marrow Transplantation--methods
Humans
Iduronidase--deficiency
Immunoglobulin G--immunology
Mucopolysaccharidosis I--drug therapy
Phenotype