Efficacy of an adeno-associated virus 8-pseudotyped vector in glycogen storage disease type II.

Sun, Baodong

Efficacy of an adeno-associated virus 8-pseudotyped vector in glycogen storage disease type II. [electronic resource] - Molecular therapy : the journal of the American Society of Gene Therapy Jan 2005 - 57-65 p. digital

Publication Type: Journal Article; Research Support, Non-U.S. Gov't; Research Support, U.S. Gov't, P.H.S.

1525-0016

10.1016/j.ymthe.2004.10.004 doi


Animals
Cell Line
Dependovirus--genetics
Female
Gene Expression Regulation
Genetic Therapy--instrumentation
Genetic Vectors--genetics
Glucan 1,4-alpha-Glucosidase--administration & dosage
Glucose--chemistry
Glycogen Storage Disease Type II--enzymology
Humans
Male
Mice
Mice, Knockout
Motor Activity
Sex Characteristics
alpha-Glucosidases