Validation in mesenchymal progenitor cells of a mutation-independent ex vivo approach to gene therapy for osteogenesis imperfecta.
Millington-Ward, Sophia
Validation in mesenchymal progenitor cells of a mutation-independent ex vivo approach to gene therapy for osteogenesis imperfecta. [electronic resource] - Human molecular genetics Sep 2002 - 2201-6 p. digital
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
0964-6906
10.1093/hmg/11.19.2201 doi
Bone Marrow--physiology
Collagen--genetics
Collagen Type I
Collagen Type I, alpha 1 Chain
Down-Regulation
Genetic Therapy
Genetic Vectors
Humans
Mesoderm--physiology
Osteogenesis Imperfecta--genetics
Polymorphism, Genetic
RNA, Catalytic--metabolism
RNA, Messenger--metabolism
Retroviridae--genetics
Validation in mesenchymal progenitor cells of a mutation-independent ex vivo approach to gene therapy for osteogenesis imperfecta. [electronic resource] - Human molecular genetics Sep 2002 - 2201-6 p. digital
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
0964-6906
10.1093/hmg/11.19.2201 doi
Bone Marrow--physiology
Collagen--genetics
Collagen Type I
Collagen Type I, alpha 1 Chain
Down-Regulation
Genetic Therapy
Genetic Vectors
Humans
Mesoderm--physiology
Osteogenesis Imperfecta--genetics
Polymorphism, Genetic
RNA, Catalytic--metabolism
RNA, Messenger--metabolism
Retroviridae--genetics