New prospects for the treatment of lysosomal storage diseases.
Schiffmann, Raphael
New prospects for the treatment of lysosomal storage diseases. [electronic resource] - Drugs 2002 - 733-42 p. digital
Publication Type: Journal Article; Research Support, U.S. Gov't, P.H.S.; Review
0012-6667
10.2165/00003495-200262050-00002 doi
Bone Marrow Transplantation
Fabry Disease--therapy
Gaucher Disease--therapy
Genetic Therapy
Glucosylceramidase--therapeutic use
Humans
Lysosomal Storage Diseases--therapy
Mucopolysaccharidoses--therapy
New prospects for the treatment of lysosomal storage diseases. [electronic resource] - Drugs 2002 - 733-42 p. digital
Publication Type: Journal Article; Research Support, U.S. Gov't, P.H.S.; Review
0012-6667
10.2165/00003495-200262050-00002 doi
Bone Marrow Transplantation
Fabry Disease--therapy
Gaucher Disease--therapy
Genetic Therapy
Glucosylceramidase--therapeutic use
Humans
Lysosomal Storage Diseases--therapy
Mucopolysaccharidoses--therapy