New prospects for the treatment of lysosomal storage diseases.

Schiffmann, Raphael

New prospects for the treatment of lysosomal storage diseases. [electronic resource] - Drugs 2002 - 733-42 p. digital

Publication Type: Journal Article; Research Support, U.S. Gov't, P.H.S.; Review

0012-6667

10.2165/00003495-200262050-00002 doi


Bone Marrow Transplantation
Fabry Disease--therapy
Gaucher Disease--therapy
Genetic Therapy
Glucosylceramidase--therapeutic use
Humans
Lysosomal Storage Diseases--therapy
Mucopolysaccharidoses--therapy