Aminoglycoside treatment for muscular dystrophy is scientifically rational, but is it clinically effective?

Hirano, Michio

Aminoglycoside treatment for muscular dystrophy is scientifically rational, but is it clinically effective? [electronic resource] - Current neurology and neuroscience reports Jan 2002 - 53-4 p. digital

Publication Type: Journal Article

1528-4042

10.1007/s11910-002-0053-y doi


Aminoglycosides--therapeutic use
Codon, Nonsense--drug effects
Codon, Terminator--genetics
Dystrophin--genetics
Humans
Muscular Dystrophy, Duchenne--drug therapy
Pilot Projects
Treatment Outcome