Nonviral transfer of the gene encoding coagulation factor VIII in patients with severe hemophilia A.
Roth, D A
Nonviral transfer of the gene encoding coagulation factor VIII in patients with severe hemophilia A. [electronic resource] - The New England journal of medicine Jun 2001 - 1735-42 p. digital
Publication Type: Clinical Trial; Clinical Trial, Phase I; Journal Article; Research Support, Non-U.S. Gov't
0028-4793
10.1056/NEJM200106073442301 doi
Adult
Aged
Biopsy
Clone Cells
Factor VIII--genetics
Fibroblasts--transplantation
Genetic Therapy--methods
Hemophilia A--genetics
Hemorrhage--epidemiology
Humans
Laparoscopy
Middle Aged
Omentum
Plasmids--genetics
Skin--cytology
Transfection--methods
Transplantation, Autologous
Nonviral transfer of the gene encoding coagulation factor VIII in patients with severe hemophilia A. [electronic resource] - The New England journal of medicine Jun 2001 - 1735-42 p. digital
Publication Type: Clinical Trial; Clinical Trial, Phase I; Journal Article; Research Support, Non-U.S. Gov't
0028-4793
10.1056/NEJM200106073442301 doi
Adult
Aged
Biopsy
Clone Cells
Factor VIII--genetics
Fibroblasts--transplantation
Genetic Therapy--methods
Hemophilia A--genetics
Hemorrhage--epidemiology
Humans
Laparoscopy
Middle Aged
Omentum
Plasmids--genetics
Skin--cytology
Transfection--methods
Transplantation, Autologous