In utero and postnatal VX-770 administration rescues multiorgan disease in a ferret model of cystic fibrosis.

In utero and postnatal VX-770 administration rescues multiorgan disease in a ferret model of cystic fibrosis. — المؤلف: Sun, Xingshen — Science translational medicine 20200427

المؤلف
Sun, Xingshen
النشر
Science translational medicine 20200427
الموضوعات
Aminophenols؛ Animals؛ Animals, Genetically Modified؛ Animals, Newborn؛ Blood Glucose؛ Chloride Channel Agonists؛ Cystic Fibrosis؛ Cystic Fibrosis Transmembrane Conductance Regulator