In utero and postnatal VX-770 administration rescues multiorgan disease in a ferret model of cystic fibrosis.
In utero and postnatal VX-770 administration rescues multiorgan disease in a ferret model of cystic fibrosis. — المؤلف: Sun, Xingshen — Science translational medicine 20200427
- المؤلف
- Sun, Xingshen
- النشر
- Science translational medicine 20200427
- الموضوعات
- Aminophenols؛ Animals؛ Animals, Genetically Modified؛ Animals, Newborn؛ Blood Glucose؛ Chloride Channel Agonists؛ Cystic Fibrosis؛ Cystic Fibrosis Transmembrane Conductance Regulator