Improved efficacy of a next-generation ERT in murine Pompe disease.

Improved efficacy of a next-generation ERT in murine Pompe disease. — المؤلف: Xu, Su — JCI insight 20200601

المؤلف
Xu, Su
النشر
JCI insight 20200601
الموضوعات
1-Deoxynojirimycin؛ Animals؛ Disease Models, Animal؛ Enzyme Replacement Therapy؛ Female؛ Glycogen؛ Glycogen Storage Disease Type II؛ Humans