Antisense oligonucleotide-mediated ataxin-1 reduction prolongs survival in SCA1 mice and reveals disease-associated transcriptome profiles.

Antisense oligonucleotide-mediated ataxin-1 reduction prolongs survival in SCA1 mice and reveals disease-associated transcriptome profiles. — المؤلف: Friedrich, Jillian — JCI insight 20191121

المؤلف
Friedrich, Jillian
النشر
JCI insight 20191121
الموضوعات
Animals؛ Ataxin-1؛ Female؛ Magnetic Resonance Spectroscopy؛ Male؛ Mice؛ Nerve Tissue Proteins؛ Neurodegenerative Diseases