Recombinant adeno-associated virus vector-based gene transfer for defects in oxidative metabolism. [electronic resource]
Producer: 20001109Description: 2067-78 p. digitalISSN:- 1043-0342
- Acidosis, Lactic -- congenital
- Adenosine Triphosphatases -- metabolism
- Animals
- Cell Line
- Cell Nucleus -- metabolism
- DNA, Mitochondrial -- genetics
- Dependovirus -- genetics
- Gene Transfer Techniques
- Genes, Reporter
- Genetic Therapy -- methods
- Genetic Vectors
- Green Fluorescent Proteins
- Humans
- Luminescent Proteins -- biosynthesis
- Microscopy, Fluorescence
- Mitochondria -- metabolism
- Mitochondrial Proton-Translocating ATPases
- Models, Genetic
- Mutation
- Neurons -- metabolism
- Oxygen -- metabolism
- Pyruvate Dehydrogenase Complex -- chemistry
- Pyruvate Dehydrogenase Complex Deficiency Disease
- Rats
- Recombinant Fusion Proteins -- metabolism
- Spinal Cord -- metabolism
- Transduction, Genetic
- Transfection
- Tumor Cells, Cultured
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Publication Type: Journal Article; Research Support, U.S. Gov't, P.H.S.
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